SGN Research Roadmap

Stages Links :
Clinical trials phases 

 

Symptomatic Treatments Links:

 

Fenfluramine for DEE

 

Skyway study for Lennox-Gastaut Syndrome

 

Rosuvatatin – Kluger

 

Lovastatin – Cook

 

Drug Screen – Rumbaugh

 

Novel Therapeutics – Clement

 

Drug Screen – Bayes (TREAT-SNGAP)

 

Drug screen iPSCs – Schmitz and Schülke

 

Cures Links:

 

ASO – Stoke Therapeutics

 

ASO – Praxis Inc.

 

ASO – Huganir

 

ASO – Prosser (Ionis)

 

ASO – CAMP4

 

AAV – Cobb and Kind

 

AAV & dCas & RE – Regel Therapeutics

 

mRNA Amplifier – Coller